Eliglustat on Gaucher Disease Type IIIB

NACompletedINTERVENTIONAL
Enrollment

4

Participants

Timeline

Start Date

April 23, 2018

Primary Completion Date

September 11, 2020

Study Completion Date

September 11, 2020

Conditions
Gaucher Disease, Type III
Interventions
DRUG

Eliglustat

"1. This is a 3-year study and the enrollment time of this study is 24 months.~2. The participants have to receive the investigational agent, Cerdelga~3. The participants have to go back to the hospital and receive the investigational agent and take the test before receving Cerdelga, and 2 weeks, 1, 3, 6, 12, 18 and 24 months after receiving Cerdelga.~4. IMP Administration Method: Cerdelga have 21 mg、42 mg and 84 mg capsule.~5. No need for fasting before use, but can't take with grapefruit juice.~6. Five ml Blood and 10 ml urine shoud be taken before receiving Cerdelga, and 1, 3, 6, 12, 18 and 24 months after receiving Cerdelga for Gaucher related biomarkers test."

Trial Locations (1)

10041

National Taiwan University Hospital, Taipei

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Sanofi

INDUSTRY

lead

National Taiwan University Hospital

OTHER

NCT03519646 - Eliglustat on Gaucher Disease Type IIIB | Biotech Hunter | Biotech Hunter