63
Participants
Start Date
March 31, 2018
Primary Completion Date
July 31, 2019
Study Completion Date
July 31, 2019
Emory University Department of Human Genetics, Decatur
University of Florida, Gainesville
Ege University School of Medicine, Izmir
Hospital of Padova, Padua
Bretonneau Hospital, Internal Medicine Department, Tours
Ann and Robert H Lurie Children's Hospital, Chicago
Necker Children's Hospital, Paris
Boston Children's Hospital, Boston
Adult Metabolic Diseases Clinic, Vancouver General Hospital, Vancouver
University Klinik Jena, Klinik für Neuropädiatrie, Jena
Rheumatology Unit, Clinic for Inborn Errors of Metabolism, Leipzig
Hacettepe University, Ankara
Umberto I Polyclinic of Rome, Roma
National Hospital for Neurology and Neurosurgery, London
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY