A Non-Interventional Interview Study of Phenylketonuria (PKU) Adults

CompletedOBSERVATIONAL
Enrollment

63

Participants

Timeline

Start Date

March 31, 2018

Primary Completion Date

July 31, 2019

Study Completion Date

July 31, 2019

Conditions
Phenylketonuria (PKU)
Trial Locations (14)

30033

Emory University Department of Human Genetics, Decatur

32610

University of Florida, Gainesville

35040

Ege University School of Medicine, Izmir

35128

Hospital of Padova, Padua

37044

Bretonneau Hospital, Internal Medicine Department, Tours

60614

Ann and Robert H Lurie Children's Hospital, Chicago

75743

Necker Children's Hospital, Paris

02115

Boston Children's Hospital, Boston

Unknown

Adult Metabolic Diseases Clinic, Vancouver General Hospital, Vancouver

University Klinik Jena, Klinik für Neuropädiatrie, Jena

Rheumatology Unit, Clinic for Inborn Errors of Metabolism, Leipzig

Hacettepe University, Ankara

00185

Umberto I Polyclinic of Rome, Roma

WC1N 3BG

National Hospital for Neurology and Neurosurgery, London

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY