Study of Dose Confirmation and Safety of Crizanlizumab in Pediatric Sickle Cell Disease Patients

PHASE2CompletedINTERVENTIONAL
Enrollment

117

Participants

Timeline

Start Date

October 1, 2018

Primary Completion Date

November 6, 2024

Study Completion Date

November 6, 2024

Conditions
Sickle Cell Disease (SCD)
Interventions
DRUG

Crizanlizumab

Crizanlizumab (SEG101) is a concentrate for solution for infusion, i.v. use. Supplied in single use 10 mL vials at a concentration of 10 mg/mL. One vial contains 100 mg of crizanlizumab.

Trial Locations (35)

123

Novartis Investigative Site, Muscat

1000

Novartis Investigative Site, Brussels

1020

Novartis Investigative Site, Laken

1434

Novartis Investigative Site, Tripoli

4000

Novartis Investigative Site, Liège

10043

Novartis Investigative Site, Orbassano

10467

Childrens Hospital at Montefiore, The Bronx

20010

Childrens National Hospital, Washington D.C.

27710

Duke University Medical Center, Durham

27834

East Carolina University, Greenville

28009

Novartis Investigative Site, Madrid

29425

Medical Uni of South Carolina, Charleston

30342

Childrens Healthcare of Atlanta, Atlanta

32610

University of Florida, Gainesville

33021

Joe DiMaggio Childrens Hospital, Hollywood

33110

Novartis Investigative Site, Mersin

35128

Novartis Investigative Site, Padua

35233

University Of Alabama, Birmingham

69120

Novartis Investigative Site, Heidelberg

75015

Novartis Investigative Site, Paris

76104

Cook Childrens Medical Center, Fort Worth

230004

Novartis Investigative Site, Montería

440009

Novartis Investigative Site, Nagpur

760012

Novartis Investigative Site, Santiago de Cali

02115

Childrens Hosp Boston Dept of Hematology, Boston

19104-4399

Childrens Hospital Of Philadelphia, Philadelphia

41253-190

Novartis Investigative Site, Salvador

14048-900

Novartis Investigative Site, Ribeirão Preto

01232-010

Novartis Investigative Site, São Paulo

H3T 1C5

Novartis Investigative Site, Montreal

1107 2020

Novartis Investigative Site, Beirut

07120

Novartis Investigative Site, Palma de Mallorca

08035

Novartis Investigative Site, Barcelona

01330

Novartis Investigative Site, Adana

SE1 7EH

Novartis Investigative Site, London

Sponsors
All Listed Sponsors
lead

Novartis Pharmaceuticals

INDUSTRY