A Study of Ravulizumab (ALXN1210) in Children and Adolescents With Paroxysmal Nocturnal Hemoglobinuria

PHASE3CompletedINTERVENTIONAL
Enrollment

13

Participants

Timeline

Start Date

February 22, 2018

Primary Completion Date

March 25, 2020

Study Completion Date

August 25, 2022

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
BIOLOGICAL

Ravulizumab

Single intravenous (IV) loading dose on Day 1, followed by regular IV maintenance dosing beginning on Day 15, based on weight.

Trial Locations (9)

30329

Clinical Trial Site, Atlanta

53226

Clinical Trial Site, Milwaukee

Unknown

Clinical Trial Site, Paris

Clinical Trial Site, Utrecht

Clinical Trial Site, Oslo

Clinical Trial Site, Moscow

Clinical Trial Site, Saint Petersburg

Clinical Trial Site, Leeds

Clinical Trial Site, London

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY