Efficacy and Safety of ALXN1840 Administered for 48 Weeks Versus Standard of Care in Participants With Wilson Disease

PHASE3TerminatedINTERVENTIONAL
Enrollment

214

Participants

Timeline

Start Date

February 22, 2018

Primary Completion Date

June 30, 2023

Study Completion Date

June 30, 2023

Conditions
Wilson Disease
Interventions
DRUG

ALXN1840

ALXN1840 administered orally in 15 mg tablets

DRUG

SoC Therapy

Depending on the site/region, participants randomized to receive SoC treatment will receive trientine, penicillamine, Zinc, or a combination of these medicines, administered according to standard regimens.

Trial Locations (56)

333

Research Site, Taoyuan

852

Research Site, Hong Kong

1010

Research Site, Grafton

1083

Research Site, Budapest

1090

Research Site, Vienna

2139

Research Site, Concord

3050

Research Site, Parkville

5000

Research Site, Adelaide

6020

Research Site, Innsbruck

8036

Research Site, Graz

8200

Research Site, Århus N

10002

Research Site, Taipei

11000

Research Site, Belgrade

20099

Research Site, Hamburg

29011

Research Site, Málaga

34010

Research Site, Istanbul

34093

Research Site, Istanbul

35100

Research Site, Izmir

41944

Research Site, Daegu

48109

Research Site, Ann Arbor

60611

Research Site, Chicago

69667

Research Site, Bron

75010

Research Site, Paris

77030

Research Site, Houston

90095

Research Site, Los Angeles

98105

Research Site, Seattle

115446

Research Site, Moscow

117292

Research Site, Moscow

119021

Research Site, Moscow

169608

Research Site, Singapore

194017

Research Site, Saint Petersburg

603005

Research Site, Nizhny Novgorod

5265601

Research Site, Ramat Gan

9112001

Research Site, Jerusalem

06510

Research Site, New Haven

VIC 3052

Research Site, Parkville

M5G 2C4

Research Site, Toronto

128 08

Research Site, Prague

69120, DE

Research Site, Heidelberg

04103

Research Site, Leipzig

266-0007

Research Site, Chiba

860-8556

Research Site, Kumamoto

830-0011

Research Site, Kurume-shi

790-0024

Research Site, Matsuyama

153-8515

Research Site, Meguro-ku

063-0005

Research Site, Sapporo

569-8686

Research Site, Takatsuki-shi

230-8765

Research Site, Yokohama

02-957

Research Site, Warsaw

04-730

Research Site, Warsaw

08036

Research Site, Barcelona

08208

Research Site, Sabadell

06230

Research Site, Ankara

B15 2WB

Research Site, Edgbaston

GU2 7WG

Research Site, Guildford

SE5 9RS

Research Site, London

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY