Phase I Study of APX005M in Pediatric Central Nervous System Tumors

PHASE1Active, not recruitingINTERVENTIONAL
Enrollment

32

Participants

Timeline

Start Date

March 1, 2018

Primary Completion Date

September 30, 2023

Study Completion Date

November 1, 2025

Conditions
Glioblastoma MultiformeHigh-grade Astrocytoma Not Otherwise Specified (NOS)CNS Primary Tumor, Not Otherwise Specified (NOS)Ependymoma, Not Otherwise Specified (NOS)Diffuse Intrinsic Pontine Gliomas (DIPG)Medulloblastoma
Interventions
BIOLOGICAL

APX005M treatment for recurrent or refractory primary malignant CNS tumor patients

"APX005M dosing will begin at 0.1 mg/kg, the APX005M dose may be increased (0.3, 0.45, 0.6 mg/kg) or decreased (0.03 mg/kg) in subsequent cohorts until the maximum tolerated dose (MTD) is reached or until dose level 3 (0.6 mg/kg) is complete without the MTD being defined.~APX005M will be administered at the assigned dose level every 21 days (3 weeks). Patients may continue to receive APX005M for 36 courses (approximately 2 years) or until disease progression, unacceptable toxicity or death, whichever occurs first."

BIOLOGICAL

APX005M treatment for newly diagnosed DIPG patients

"The starting dose of APX005M for the DIPG patients will be one dose level below the recommended phase II dose (RP2D) determined in Stratum 1 patients. The dose may be decreased or increased to the RP2D established in Stratum 1.~APX005M will be administered at the assigned dose level every 21 days (3 weeks). Patients may continue to receive APX005M for 36 courses (approximately 2 years) or until disease progression, unacceptable toxicity or death, whichever occurs first."

Trial Locations (11)

10065

Memorial Sloan Kettering Cancer Center, New York

15224

Children Hospital of Pittsburgh of UPMC, Pittsburgh

30322

Children's Healthcare of Atlanta, Atlanta

38105

St. Jude Children Research Hospital, Memphis

45229

Cincinnati Children Hospital Medical Center, Cincinnati

60614

Lurie Childrens Hospital-Chicago, Chicago

77030

Baylor College of Medicine, Houston

80045

Children's Hospital Colorado, Aurora

90026

Children's Hospital Los Angeles, Los Angeles

94304

Lucile Packard Children Hospital Stanford University, Palo Alto

20010-2970

Childrens National Medical Center, Washington D.C.

All Listed Sponsors
collaborator

American Lebanese Syrian Associated Charities

OTHER

collaborator

Pyxis Oncology, Inc

INDUSTRY

collaborator

Solving Kids' Cancer

OTHER

collaborator

Ty Louis Campbell Foundation

OTHER

collaborator

A Kids' Brain Tumor Cure Foundation

OTHER

collaborator

National Cancer Institute (NCI)

NIH

lead

Pediatric Brain Tumor Consortium

NETWORK

NCT03389802 - Phase I Study of APX005M in Pediatric Central Nervous System Tumors | Biotech Hunter | Biotech Hunter