206
Participants
Start Date
October 24, 2017
Primary Completion Date
December 31, 2029
Study Completion Date
December 31, 2029
Givinostat
suspension of givinostat (10 mg/mL)
Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette, Paris
Leiden University Medical Center LUMC, Albinusdreef 2, Leiden
Radboud University Medical Centre, Nijmegen
Clinic of Neurology and Psychiatry for Children and Youth - Neurology Department Dr. Subotic 6a,, Belgrade
U.O.S.D. Centro Traslazionale di Miologia e Patologie Neurodegenerative, Building 16 - ground floor IRCCS Istituto Giannina Gaslini,, Genova
The Children's Hospital of Philadelphia Colket Translational Research Building, Philadelphia
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, UOS di Neurologia Pediatrica, Milan
IRCCS Istituto Neurologico Carlo Besta, Milan
Centro Clinico NeMO Fondazione Serena ONLUS Area SUD, Milan
Klinik- und Poliklinik fur Kinder- und Jugendmedizin, Universitatsklinikum HamburgEppendorf, Martinistr. 52, Hamburg
Virginia Commonwealth University Childrens Hospital of Richmond at, Richmond
MD Rare Disease Research, LLC, Atlanta
Child Health Research Institute, Gainesville
Hospital Universitario Virgen del Rocio, Seville
CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest, Nantes
University of Iowa Children's Hospital, Iowa City
Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111, St Louis
Klinikum der Universitat Munchen, Campus Innenstadt, Lindwurmstr. 4, München
Rady Children's Hospital center - UCSD Department of Neuroscience, San Diego
University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation, Sacramento
Shriners Hospitals for Children, Portland
A.O.U. Policlinico G. Martino, U.O.C. Neurologia e Malattie Neuromuscolari, Messina
Institute of Neurology - Schneider Children's Medical Center of Israel Kaplan, 14, Petah Tikva
Connecticut Children's Medical Center, Neurology Division, Hartford
University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology, Leuven
Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN), Liège
Kinsmen Research Centre - Alberta Children's Hospital, Calgary
The University of British Columbia, Children's and Womens Health Centre of BC Branch, Vancouver
Holland Bloorview Kids Rehabilitation Hospital, Toronto
Universitätsklinikum Essen - Kinder-und Jugendmedizin Neuropadiatrie, Essen
Ospedale Pediatrico Bambino Gesù, Malattie Neuromuscolari e Neurodegenerative, Roma
"Fondazione Policlinico Universitario A.Gemelli, UOC Neuropsichiatria Infantile", Roma
Neuromuscular Pathology Unit - Hospital Sant Joan de Déu, Esplugues de Llobregat
Hospital Materno-Infantil, Barcelona
Hospital Universitari i Politècnic La Fe - Servicio Neurologia, Valencia
Alder Hey Children's Hospital NHS Trust, Liverpool
The Robert Jones and Agnes Hunt Orthopaedic Hospital NHS Foundation Trust, Gobowen
UCL Great Ormond Street Institute of Child Health, Dubowitz Neuromuscular Centre and MRC Centre for NMD, London
The John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne
Lead Sponsor
Collaborators (1)
Cromsource
INDUSTRY
Italfarmaco
INDUSTRY