Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

PHASE2/PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

206

Participants

Timeline

Start Date

October 24, 2017

Primary Completion Date

December 31, 2029

Study Completion Date

December 31, 2029

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

Givinostat

suspension of givinostat (10 mg/mL)

Trial Locations (39)

760

Hôpital Armand Trousseau I-Motion - Plateforme d'essais cliniques pédiatriques Bâtiment Lemariey - Porte 20 * 2ème étage 26 Avenue du Dr Arnold Nette, Paris

2300

Leiden University Medical Center LUMC, Albinusdreef 2, Leiden

6500

Radboud University Medical Centre, Nijmegen

11000

Clinic of Neurology and Psychiatry for Children and Youth - Neurology Department Dr. Subotic 6a,, Belgrade

16147

U.O.S.D. Centro Traslazionale di Miologia e Patologie Neurodegenerative, Building 16 - ground floor IRCCS Istituto Giannina Gaslini,, Genova

19104

The Children's Hospital of Philadelphia Colket Translational Research Building, Philadelphia

20122

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico di Milano, UOS di Neurologia Pediatrica, Milan

20133

IRCCS Istituto Neurologico Carlo Besta, Milan

20162

Centro Clinico NeMO Fondazione Serena ONLUS Area SUD, Milan

20246

Klinik- und Poliklinik fur Kinder- und Jugendmedizin, Universitatsklinikum HamburgEppendorf, Martinistr. 52, Hamburg

23298

Virginia Commonwealth University Childrens Hospital of Richmond at, Richmond

30318

MD Rare Disease Research, LLC, Atlanta

32610

Child Health Research Institute, Gainesville

41013

Hospital Universitario Virgen del Rocio, Seville

44093

CHU de Nantes - Hotel-Dieu - Hopital Nord Laennec, rez-de-chausse haut ail Ouest, Nantes

52242

University of Iowa Children's Hospital, Iowa City

63110

Washington University School of Medicine in St Louis Department of Neurology 660 S.Euclid Avenue, Campus Box 8111, St Louis

80337

Klinikum der Universitat Munchen, Campus Innenstadt, Lindwurmstr. 4, München

92123

Rady Children's Hospital center - UCSD Department of Neuroscience, San Diego

95817

University of California - Davis Medical Center - Devis Physical Medicine & Rehabilitation, Sacramento

97239

Shriners Hospitals for Children, Portland

98125

A.O.U. Policlinico G. Martino, U.O.C. Neurologia e Malattie Neuromuscolari, Messina

4920235

Institute of Neurology - Schneider Children's Medical Center of Israel Kaplan, 14, Petah Tikva

06106

Connecticut Children's Medical Center, Neurology Division, Hartford

03000

University Hospitals Leuven, Neuromuscular Reference Centre, Child Neurology, Leuven

04000

Hospital de La Citadelle, Centre de Référence des Maladies Neuromuscolaires (CRMN), Liège

T3B 6A8

Kinsmen Research Centre - Alberta Children's Hospital, Calgary

V6H 3V4

The University of British Columbia, Children's and Womens Health Centre of BC Branch, Vancouver

M4G1R8

Holland Bloorview Kids Rehabilitation Hospital, Toronto

D-45147

Universitätsklinikum Essen - Kinder-und Jugendmedizin Neuropadiatrie, Essen

00146

Ospedale Pediatrico Bambino Gesù, Malattie Neuromuscolari e Neurodegenerative, Roma

00168

"Fondazione Policlinico Universitario A.Gemelli, UOC Neuropsichiatria Infantile", Roma

08950

Neuromuscular Pathology Unit - Hospital Sant Joan de Déu, Esplugues de Llobregat

08035

Hospital Materno-Infantil, Barcelona

Unknown

Hospital Universitari i Politècnic La Fe - Servicio Neurologia, Valencia

L12 2AP

Alder Hey Children's Hospital NHS Trust, Liverpool

SY10 7AG

The Robert Jones and Agnes Hunt Orthopaedic Hospital NHS Foundation Trust, Gobowen

, WC1N 1EH

UCL Great Ormond Street Institute of Child Health, Dubowitz Neuromuscular Centre and MRC Centre for NMD, London

NE1 3BZ

The John Walton Muscular Dystrophy Research Centre, Newcastle upon Tyne

Sponsors

Lead Sponsor

Collaborators (1)

All Listed Sponsors
collaborator

Cromsource

INDUSTRY

lead

Italfarmaco

INDUSTRY