144
Participants
Start Date
December 19, 2017
Primary Completion Date
November 16, 2020
Study Completion Date
November 20, 2024
valoctocogene roxaparvovec
Adeno-Associated Virus Vector-Mediated Gene Transfer of Human Factor VIII in Hemophilia A
UNC Hemophilia and Thrombosis Center, Chapel Hill
St. Joseph's Children's Hospital, Center for Bleeding and Clotting Disorders, Tampa
James Graham Brown Cancer Center, Louisville
Nationwide Children's Hospital, Columbus
Wayne State University, Detroit Medical Center, Detroit
University of Minnesota, Minneapolis
University of Colorado, Aurora
University of California San Diego, Hematology and Oncology, Hemophilia &Thrombosis Treatment Center, San Diego
UC Davis Hemophilia Treatment Center, Sacramento
Los Angeles Orthopedic Hospital, Orthopedic Hemophilia Treatment Center, Los Angeles
UCSF Medical Center, San Francisco
Ann & Robert H. Lurie Children's Hospital of Chicago, Department of Hematology, Chicago
Tulane University Hematology & Medical Oncology, New Orleans
University of Michigan, Pediatric Hematology and Oncology, Ann Arbor
Washington University School of Medicine, Department of Pediatrics, Division of Hematology/Oncology, St Louis
The Royal Adelaide Hospital (RAH), Adelaide
Royal Brisbane and Women's Hospital, Brisbane
Alfred Hospital, Melbourne
Fiona Stanley Hospital, Perth
Royal Prince Alfred Hospital, Sydney
University Hospital Leuven, Leuven
Campinas Estadual University (UNICAMP) / Campinas Hemocentro / Hematologia E Hemoterapia Center, Campinas
Parana's Hematology And Hemotherapy Center (HEMEPAR), Curitiba
Arthur De Siqueira Cavalcanti Hematology State Institute, Rio de Janeiro
Sao Paulo University Clinical Hospital, São Paulo
Holy Spirit Hematology and Hemotherapy Center, Vitória
Regional University Hospital of Lille (CHRU de Lille), Lille
Hopital de la Timone Marseille - Assistance Publique des Hopitaux de Marseille, Marseille
Vivantes Clinic im Friedrichshain- Landsberger Allee, Berlin
University Clinic Bonn, Bonn
Chaim Sheba Medical Center, Ramat Gan
Maggiore Polyclinic Hospital, IRCCS Ca' Granda, Center for Hemophilia and Thrombosis Angelo Bianchi Bonomi, Milan
Charlotte Maxeke Johannesburg Academic Hospital, Hemophilia Comprehensive Care Center, Johannesburg
Department of Pediatrics, Kyung Hee University Hospital at Gangdong, Seoul
Hospital Teresa Herrera, A Coruña
University Hospital Virgen del Rocio (HUVR), Seville
Changhua Christian Hospital, Changhua
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Taichung Veterans General Hospital, Taichung
National Taiwan University Hospital, Taipei
Tri-Service General Hospital, Taipei
Queen Elizabeth Hospital, Birmingham
Addenbrookes Hospital, Cambridge
Glasgow Royal Infirmary, Department of Hematology, Glasgow
Barts and The London School of Medicine and Dentistry, Haemophilia Centre, London
Hammersmith, London
St Thomas' Hospital, London
Churchill Hospital, Oxford Hemophilia and Thrombosis Center, Oxford
University Hospital Southampton NHS Foundation Trust, Southampton
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY