NCT03368742View on ClinicalTrials.gov

Microdystrophin Gene Transfer Study in Adolescents and Children With DMD

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

December 6, 2017

Primary Completion Date

October 15, 2026

Study Completion Date

October 15, 2026

Conditions
Duchenne Muscular Dystrophy
Interventions
GENETIC

SGT-001

AAV9 vector containing muscle-specific promoter and microdystrophin construct

Trial Locations (2)

32610

University of Florida, Gainesville

90095

David Geffen School of Medicine at UCLA, Los Angeles

All Listed Sponsors
lead

Solid Biosciences Inc.

INDUSTRY

NCT03368742 - Microdystrophin Gene Transfer Study in Adolescents and Children With DMD | Biotech Hunter | Biotech Hunter