60
Participants
Start Date
May 28, 2017
Primary Completion Date
September 30, 2021
Study Completion Date
September 30, 2021
Standardized strength, respiratory and motor function assessments
Standardized assessments will be adjusted by the age, the ambulant status and the respiratory status of the patient. The visit frequency will also be adjusted according to the age and to the time spent in the study varying between quarterly to yearly.
Centre de référence neuromusculaire, CHR La Citadelle, Liège
Hôpital Roger Salengro, CHU Lille, Lille
Hôpital de la Croix Rousse, Lyon
Hôpital Femme Mère Enfant, CHU Lyon L'Escale, Bron
Hôpital Armand Trousseau, Paris
I-Motion Institute - Trousseau Hospital, Paris
Institute of Myology, Paris
Hôpital Sainte Musse, Toulon
Universitätsklinikum Essen (AöR), Essen
Bambino Gesu Children's Hospital, Roma
Hospital Puerta del Mar, Cadiz
Collaborators (1)
Dynacure
INDUSTRY
Institut de Myologie, France
OTHER