Study of ORL-1B in Patients With Biotinidase Deficiency

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

20

Participants

Timeline

Start Date

August 31, 2013

Primary Completion Date

January 1, 2018

Study Completion Date

January 1, 2018

Conditions
Biotinidase Deficiency
Interventions
DRUG

ORL-1B

Oral ORL-1B

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Orpha Labs

INDUSTRY

NCT03269045 - Study of ORL-1B in Patients With Biotinidase Deficiency | Biotech Hunter | Biotech Hunter