A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

Active, not recruitingOBSERVATIONAL
Enrollment

44

Participants

Timeline

Start Date

November 16, 2017

Primary Completion Date

October 31, 2025

Study Completion Date

December 31, 2025

Conditions
Mucopolysaccharidosis Type IIIB
Trial Locations (9)

3052

Murdoch Childrens Research Institute and Royal Children's Hospital, Melbourne

10449

MacKay Memorial Children's Hospital, Taipei

15706

Hospital Clínico Universitario de Santiago, Santiago de Compostela

20246

University Medical Center Hamburg-Eppendorf, Hamburg

94609

UCSF Benioff Children's Hospital Oakland, Oakland

B1629AHJ

Hospital Universitario Austral, Pilar

90035-903

Medical Genetics Service/HCPA, Department of Genetics/UFRGS, Pôrto Alegre

Unknown

Fundación Cardio Infantil - Instituto de Cardiología, Bogotá

06560

Gazi University Faculty of Medicine, Ankara

Sponsors
All Listed Sponsors
lead

Allievex Corporation

INDUSTRY

NCT03227042 - A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) | Biotech Hunter | Biotech Hunter