Efficacy, Tolerability, and Pharmacokinetics of Multiple Doses of Oral TAK-831 in Adults With Friedreich Ataxia

PHASE2CompletedINTERVENTIONAL
Enrollment

67

Participants

Timeline

Start Date

November 8, 2017

Primary Completion Date

December 27, 2018

Study Completion Date

December 27, 2018

Conditions
Friedreich Ataxia
Interventions
DRUG

TAK-831

TAK-831 tablets

DRUG

TAK-831 Placebo

TAK-831 placebo matching tablets

Trial Locations (6)

19104

The Children's Hospital of Philadelphia, Philadelphia

32607

University of Florida Center for Movement Disorders, Gainesville

33612

USF College of Medicine, Tampa

43220

Ohio State University Wexner Medical Center, Columbus

52242

University of Iowa Children's Hospital, Iowa City

90095

UCLA Ataxia Center, Los Angeles

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Takeda

INDUSTRY

lead

Neurocrine Biosciences

INDUSTRY