121
Participants
Start Date
December 12, 2016
Primary Completion Date
October 30, 2019
Study Completion Date
October 30, 2019
BMN 111
Subcutaneous injection of 15 μg/kg of BMN 111 daily
Placebo
Subcutaneous injection of 15 μg/kg of placebo daily
The Children's Hospital at Westmead, Westmead
Murdoch Children's Research Institute, Parkville
Alfred I. duPont Hospital for Children, Wilmington
Johns Hopkins University, Baltimore
Hospital Universitario Virgen de la Victoria, Málaga
Emory University, Decatur
Acibadem University School of Medicine, Istanbul
Otto-von-Guericke Universitaet, Universitaetskinderklinik, Magdeburg
Cincinnati Children's Hospital Medical Center, Cincinnati
Universitätsklinikum Münster, Münster
Medical College of Wisconsin, Children's Hospital, Milwaukee
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
University of Missouri, Columbia
Baylor College of Medicine, Houston
Harbor - UCLA Medical Center, Torrance
Children's Hospital & Research Center Oakland, Oakland
Seattle Children's Hospital, Seattle
Osaka University Hospital, Osaka
Saitama Children's Medical Center, Saitama
Tokushima University Hospital, Tokushima
Institut Catala de Traumatologica I Medicina de l'Esport, Barcelona
Hospital Sant Joan de Deu, Barcelona
Guy's and St. Thomas NHS Foundation Trust Evelina Children's Hospital, London
Sheffield Children's NHS Foundation Trust, Sheffield
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY