Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease

CompletedOBSERVATIONAL
Enrollment

5

Participants

Timeline

Start Date

January 1, 2014

Primary Completion Date

April 30, 2014

Study Completion Date

March 30, 2017

Conditions
Enzyme Replacement Therapy in Pompe Disease
All Listed Sponsors
lead

Rambam Health Care Campus

OTHER

NCT03147664 - Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease | Biotech Hunter | Biotech Hunter