Study of Ravulizumab in Children and Adolescents With Atypical Hemolytic Uremic Syndrome (aHUS)

PHASE3CompletedINTERVENTIONAL
Enrollment

34

Participants

Timeline

Start Date

August 31, 2017

Primary Completion Date

December 20, 2022

Study Completion Date

December 20, 2022

Conditions
Atypical Hemolytic Uremic Syndrome (aHUS)
Interventions
BIOLOGICAL

Ravulizumab

Participant received weight-based dosages for 26 weeks during the Initial Evaluation Period. Participants received a loading dose on Day 1, followed by maintenance dosing on Day 15 and once every 8 weeks thereafter for participants weighing ≥ 20 kg, or once every 4 weeks for participant weighing \< 20 kg.

Trial Locations (18)

1020

Research Site, Brussels

8035

Research Site, Barcelona

8950

Research Site, Esplugues de Llobregat

15006

Research Site, A Coruña

20122

Research Site, Milan

28203

Research Site, Charlotte

30322

Research Site, Atlanta

33021

Research Site, Hollywood

46026

Research Site, Valencia

48201

Research Site, Detroit

50612

Research Site, Yangsan

63241

Research Site, Jeju-do

68198

Research Site, Omaha

69120

Research Site, Heidelberg

07601

Research Site, Hackensack

03080

Research Site, Seoul

G3 8SJ

Research Site, Glasgow

WC1N 3JH

Research Site, London

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY