A Study of the Dosing, Efficacy, and Safety of Oral Cysteamine in Adult Patients With Cystic Fibrosis Exacerbations

PHASE2CompletedINTERVENTIONAL
Enrollment

91

Participants

Timeline

Start Date

December 31, 2016

Primary Completion Date

April 30, 2018

Study Completion Date

April 30, 2018

Conditions
Cystic Fibrosis
Interventions
DRUG

Cysteamine

Oral Cysteamine Capsule

DRUG

Placebo Oral Capsule

Placebo Oral Capsule

Trial Locations (17)

12208

Albany Medical College, Albany

26506

West Virginia University, Morgantown

32610

University of Florida, Gainesville

32803

Central Florida Pulmonary, Orlando

37126

Azienda Ospedaliera Universitaria Integrato di Verona Borgo Trento Centro Fibrosi Cistica, Verona

43205

Nationwide Children's Hospital, Columbus

53226

The Medical College of Wisconsin/Froedtert Hospital, Milwaukee

85724

Banner University of Arizona Medical Center, Tucson

94115

San Francisco Critical Care Medical Group California Pacific Medical Center, San Francisco

00165

Ospedale Padiatrico Bambino Gesu Centro Fibrosi Cistica, Roma

AB25 2ZN

Aberdeen Royal Infirmary, Aberdeen

DD1 9SY

Ninewells Hospital Scottish Adult Cystic Fibrosis Service, Dundee

EH4 3HE

Western General Hospital Edinburgh, CF Adults / CF Unit, Edinburgh

G51 4TF

NHS GGC, Glasgow

IV2 3UJ

Raigmore Hospital, Inverness

LS9 7TF

St. James University Hospital, Leeds

NE1 4LP

Royal Victoria Infirmary Adult CF Centre, Newcastle upon Tyne

Sponsors

Lead Sponsor

Collaborators (1)

All Listed Sponsors
collaborator

Agility Clinical, Inc.

INDUSTRY

collaborator

PSR Group B.V.

INDUSTRY

lead

NovaBiotics Ltd.

INDUSTRY