7
Participants
Start Date
April 30, 2016
Primary Completion Date
September 30, 2016
Study Completion Date
September 30, 2016
BMN 044 IV 6 mg/kg
BMN 044 IV 9 mg/kg
BMN 044 SC 6 mg/kg
Universitair Ziekenhuis Leuven, Leuven
S.Anna Hospital, Ferrara
Policlinico Univsersitario Agostino Gemelli, Rome
Drottning Silvias Barn- ochungdomssjukhus, Gothenburg
Leiden University Medical Center, Leiden
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY