Safety and Efficacy Trial of AAV Gene Therapy in Patients With CNGA3 Achromatopsia (A Clarity Clinical Trial)

PHASE1/PHASE2Active, not recruitingINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

August 3, 2017

Primary Completion Date

August 31, 2022

Study Completion Date

August 31, 2026

Conditions
Achromatopsia
Interventions
BIOLOGICAL

AGTC-402

AGTC-402 is a non-replicating, rep/cap-deleted, recombinant adeno-associated virus vector that expresses the CNGA3 gene.

Trial Locations (6)

32607

VitreoRetinal Associates, Gainesville

33136

Bascom Palmer Eye Institute, Miami

45242

Cincinnati Eye Institute, Cincinnati

91120

Hadassah-Hebrew University Medical Center, Jerusalem

97239

Casey Eye Institute, Oregon Health and Sciences University, Portland

02114

Massachusetts Eye and Ear Infirmary, Boston

Sponsors
All Listed Sponsors
lead

Beacon Therapeutics

INDUSTRY