A Study of Recombinant Von Willebrand Factor (rVWF) With or Without ADVATE in Children With Severe Von Willebrand Disease (VWD)

PHASE3RecruitingINTERVENTIONAL
Enrollment

31

Participants

Timeline

Start Date

November 6, 2017

Primary Completion Date

March 31, 2026

Study Completion Date

March 31, 2026

Conditions
Von Willebrand Disease
Interventions
BIOLOGICAL

Vonicog alfa

Lyophilized powder and solvent to prepare solution for injection.

BIOLOGICAL

Antihemophilic Factor (Recombinant)

Packaged in single boxes with 2 glass vials, with one vial containing the lyophilized ADVATE and the second vial containing the diluent.

Trial Locations (46)

1090

RECRUITING

AKH - Medizinische Universität Wien, Vienna

3000

RECRUITING

UZ Leuven, Leuven

6020

COMPLETED

Medizinische Universität Innsbruck, Innsbruck

14033

RECRUITING

CHU CAEN - Hôpital de la Côte de Nacre, Caen

19104

COMPLETED

Children's Hospital of Philadelphia, Philadelphia

20010

COMPLETED

Children's National Medical Center, Washington D.C.

20122

RECRUITING

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico, Milan

20246

COMPLETED

Universitaetsklinikum Hamburg-Eppendorf, Hamburg

27157

COMPLETED

Comprehensive Cancer Center of Wake Forest Unversity, Winston-Salem

28204

COMPLETED

St. Jude Affiliate Clinic at Novant Health, Charlotte

29425

RECRUITING

Medical University of South Carolina, Charleston

29609

COMPLETED

Hôpital Morvan, Brest

30159

COMPLETED

Werlhof-Institut GmbH, Hanover

30625

COMPLETED

Medizinische Hochschule Hannover, Hanover

32610

RECRUITING

University of Florida College of Medicine, Jacksonville

33000

RECRUITING

Groupe Hospitalier Pellegrin - Hôpital Pellegrin, Bordeaux

34098

RECRUITING

Istanbul University Cerrahpasa Medical Faculty, Istanbul

35100

RECRUITING

Ege University Medical Faculty, Izmir

43205

RECRUITING

Nationwide Children's Hospital, Columbus

44093

COMPLETED

CHU de Nantes Site Hotel Dieu, Nantes

44106

RECRUITING

Rainbow Babies and Children's Hospital, Cleveland

45229

RECRUITING

Cincinnati Children's Hospital Medical Center, Cincinnati

46026

RECRUITING

Hospital Universitari i Politecnic La Fe, Valencia

46260

COMPLETED

Indiana Hemophilia and Thrombosis Center, Indianapolis

50134

RECRUITING

Azienda Ospedaliera Universitaria Careggi, Florence

53225

COMPLETED

Comprehensive Center for Bleeding Disorders, Milwaukee

55139

RECRUITING

Ondokuz Mayis Univ. Med. Fac., Samsun

59037

RECRUITING

Hopital Cardiologique - CHU Lille, Lille

61615

RECRUITING

Bleeding and Clotting Disorders Institute, Peoria

68198

COMPLETED

University of Nebraska Medical Center, Omaha

69677

RECRUITING

Groupement Hospitalier Est- Hôpital Louis Pradel, Bron

75743

RECRUITING

Hôpital Necker - Enfants Malades, Paris

77030

RECRUITING

Texas Children's Cancer and Hematology Center, Houston

RECRUITING

Texas Children's Hospital, Houston

79044

COMPLETED

SI Institute of Blood Pathology and Transfusion Medicine of NAMSU, Lviv

80045

RECRUITING

University of Colorado Hemophilia & Thrombosis Center, Aurora

80122

RECRUITING

Azienda Ospedaliera Pediatrica Santobono Pausillipon, Napoli

94270

RECRUITING

Groupement Hospitalier Sud - Hôpital Bicêtre, Le Kremlin-Bicêtre

610027

ACTIVE_NOT_RECRUITING

"FSBI of Science Kirov Scientific and Research Institute of Hematology and Blood Transfusion of FMBA", Kirov

650066

COMPLETED

"SAIH Kemerovo Regional Clinical Hospital", Kemerovo

656038

COMPLETED

SBEI HPE Altai State Medical University of MoH and SD, Barnaul

613 00

COMPLETED

Fakultni nemocnice Brno, Brno

00165

RECRUITING

Ospedale Pediatrico Bambino Gesù, Roma

3015 CN

COMPLETED

Erasmus Medisch Centrum, Rotterdam

03010

RECRUITING

Hospital General Universitario de Alicante, Alicante

M13 9WL

COMPLETED

Royal Manchester Children's Hospital, Manchester

All Listed Sponsors
collaborator

Takeda Development Center Americas, Inc.

INDUSTRY

lead

Baxalta now part of Shire

INDUSTRY