NCT02926066 - A Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC - An Expansion | Biotech Hunter

Enrollment

Participants

Timeline

Start Date

November 9, 2016

Primary Completion Date

January 24, 2022

Study Completion Date

May 16, 2022

Conditions

Aromatic Amino Acid Decarboxylase Deficiency

Interventions

DRUG

AAV2-hAADC

"Dosage form: Aqueous solution Dose(s): 2.37x10\^11 vg/case(High dose) Dosing schedule: Intracerebral infusion, single dose Mechanism of action (if known): supplement a gene defect~Dosage form: Aqueous solution Dose(s): 1.81x10\^11 vg/case(Standard dose) Dosing schedule: Intracerebral infusion, single dose Mechanism of action (if known): supplement a gene defect"

Trial Locations (1)

100

National Taiwan University Hospital, Taipei