59
Participants
Start Date
October 13, 2016
Primary Completion Date
November 22, 2018
Study Completion Date
November 22, 2018
PF-06252616
Either 5mg/kg, 20mg/kg or 40mg/kg will be assigned to a subject based on their maximum tolerated dose from B5161002
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
UOC Farmacia - Istituto Gianna Gaslini,, Genova
UOC Medicina Fisica Riabilitativa - Istituto G. Gaslini, Genova
UOC Neurologia Pediatrica e Malattie Muscolari Istituto Gianna Gaslini, Genova
UOC Radiologia - Istituto Gianna Gaslini,, Genova
UOS Dipartimentale Endocrinologia Clinica Sperimentale - Ist., Genova
Children's Hospital of Philadelphia, Philadelphia
Kennedy Krieger Institute Out-patient Center, Baltimore
Kennedy Krieger Institute, Baltimore
Johns Hopkins Hospital, Baltimore
Johns Hopkins Investigational Drug Service, Baltimore
Duke University Medical Center, Lenox Baker Children's Hospital, Durham
Duke University, Investigational Drug Pharmacy, Durham
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Iowa ICTS, Clinical Research Unit, Iowa City
University of Minnesota Masonic Children's Hospital, Minneapolis
(For Drug deliveries) IDS Pharmacy, Minneapolis
St. Louis Childrens's Hospital, St Louis
Center for Clinical and Translational Sciences, Salt Lake City
Utah Center for Advanced Imaging and Research (UCAIR), Salt Lake City
Investigational Drug Services, Salt Lake City
Utah Program for Inherited Neuromuscular Disorder, Salt Lake City
University of Utah Hospital, Salt Lake City
University of Utah School of Medicine, Salt Lake City
David Geffen School of Medicine at UCLA/UCLA Neurology, Los Angeles
Ronald Reagan UCLA Medical Center, Los Angeles
Ronald Reagan UCLA Pharmacy, Los Angeles
UCLA (David Geffen School of Medicine), Department of Orthopedic Surgery, Los Angeles
UCLA Clinical & Translational Research Center, Los Angeles
University of California, Davis Medical Center, Sacramento
Massachusetts General Hospital, Boston
Alberta Children's Hospital, Calgary
UBC Children's and Women's Health Centre of British Columbia, Vancouver
Children's Hospital- London Health Sciences Centre, London
Centre de Readaptation Marie Enfant (CRME), Montreal
CHU Sainte-Justine, Montreal
Dipartimento Pediatrico Universitario-Ospedaliero Endocrinologia, Rome
Farmacia Ospedaliera, IRCCS Ospedale Pediatrico Bambino Gesu, Rome
IRCCS Ospedale Pediatrico Bambino Gesu - Centro Trials, Rome
U.O. Malattie Neuromuscolari e Neurodegenerative, IRCCS Ospedale Pediatrico Bambino Gesu, Rome
Hyogo college of medicine hospital, Nishinomiya-shi
National Center of Neurology and Psychiatry, Kodaira
Dubowitz Neuromuscular Centre, Institute of Child Health, London
Great Ormond Street Hospital, London
Institute of Genetic Medicine,Muscle Team, Newcastle upon Tyne
Clinical Research Facility, Newcastle upon Tyne
Royal Victoria Infirmary Research Pharmacy, Newcastle upon Tyne
Lead Sponsor
Pfizer
INDUSTRY