Clearing Lungs With ENaC Inhibition in Primary Ciliary Dyskinesia

PHASE2CompletedINTERVENTIONAL
Enrollment

123

Participants

Timeline

Start Date

August 31, 2016

Primary Completion Date

November 20, 2018

Study Completion Date

November 20, 2018

Conditions
Primary Ciliary Dyskinesia
Interventions
DRUG

VX-371

DRUG

Hypertonic Saline

DRUG

Placebo (0.17% saline)

DRUG

VX-371 + HS

DRUG

Ivacaftor

Trial Locations (34)

Unknown

Birmingham

Palo Alto

Aurora

Washington D.C.

Miami

Tampa

Chicago

Indianapolis

Iowa City

Kansas City

Boston

Ann Arbor

Minneapolis

Kansas City

St Louis

New York

Chapel Hill

Cleveland

Philadelphia

Columbia

Seattle

Toronto

Montreal

Copenhagen

Münster

Hanover

Heidelberg

Pisa

Amsterdam

Rotterdam

Rabka-Zdrój

Cambridge

London

Southampton

Sponsors

Lead Sponsor

All Listed Sponsors
collaborator

Vertex Pharmaceuticals Incorporated

INDUSTRY

lead

Parion Sciences

INDUSTRY

NCT02871778 - Clearing Lungs With ENaC Inhibition in Primary Ciliary Dyskinesia | Biotech Hunter | Biotech Hunter