255
Participants
Start Date
September 30, 2016
Primary Completion Date
December 1, 2020
Study Completion Date
December 1, 2020
Idebenone 150 mg film-coated tablets
placebo
Children's University Hospital, Dublin
Gottfried von Preyer'sches Kinderspital, Vienna
Sofia Medical University, Sofia
University Hospital Leuven, Leuven
Centre de Référence Neuromusculaire, CHR Citadelle, Liège
Center for neuromuscular disorders, Universitäts-Kinderspital beider Basel (UKBB), Basel
Radboud university medical centre, Nijmegen
Hospital Universitari Vall D' Hebron, Barcelona
Universitätsmedizin Berlin Campus Virchow-Klinikum, Berlin
University of Rochester Medical Center, Rochester
Istituto Giannina Gaslini, Genova
Universitätsklinikum Hamburg-Eppendorf, Klinik für Kinder- und Jugendmedizin, Hamburg
Johns Hopkins University, Baltimore
Fondazione IRCCS Eugenio Medea, Bosisio Parini
"Dipartimento di Clinica Neurologica e Psichiatrica dell'Età Evolutiva della Fondazione IRCCS C. Mondino di Pavia", Pavia
Hospital Universitario La Paz, Madrid
Neurosciences Institute, Neurology - Charlotte Carolinas Healthcare System, Charlotte
Rare Disease Research, Atlanta
Hôpital des enfants, Toulouse
Shriners Hospitals for Children-Tampa, Tampa
CHRU de Montpellier - Hôpital Gui de Chauliac, Montpellier
Reparto Di Neurologia dell'Osperdale Di Padova, Padua
University of Alabama, Birmingham
Hospital Universitario Virgen del Rocio, Seville
Hôpital Hôtel Dieu, Nantes
Universitätsklinikum Essen, Essen
Uniklinik Köln, Cologne
University of Iowa, Iowa City
Gillette Children's Specialty Healthcare, Saint Paul
Service de neuropédiatrie Pôle Pédiatrie CHRU de Lille - Hôpital Jeanne de Flandre, Lille
University of Kansas, Fairway
Cook Children's Medical Center, Fort Worth
"Servizio di Cardiomiologia e Genetica Medica, AOU Università degli Studi della Campania Luigi Vanvitelli", Napoli
Phoenix Children's Hospital, Phoenix
Banner University of Arizona Medical Center, Tucson
Childrens Hospital of Los Angeles, Los Angeles
David Geffen School of Medicine at UCLA, Los Angeles
Loma Linda University Healthcare, San Bernardino
UC Davis Department of Physical Medicine and Rehabilitation, Sacramento
Scientific Coordinator Nemo Sud Clinical Center, Messina
Institute of Neurology at Schneider Children's Medical Center of Israel, Petah Tikva
Children's Hospital Boston, Boston
Cincinnati Children's Hospital, Cincinnati
MetroHealth Medical Center, Cleveland
Children's Hospital of Philadelphia, Philadelphia
I-Motion - Plateforme d'essais cliniques pédiatriques Hôpital Armand Trousseau bâtiment Lemariey porte 20, Paris
Universitätsklinik Freiburg Zentrum für Kinderheilkunde und Jugendmedizin, Freiburg im Breisgau
Universitätsklinikum Heidelberg Zentrum für Kinder- und Jugendmedizin, Heidelberg
Zentrum für neuromuskuläre Erkrankungen, München
Semmelweis University 2nd Department of Paediatrics, Budapest
Centro Clinico NEMO (NEuroMuscular Omnicentre), Niguarda Hospital, Milan
LUMC, Leiden
Sahlgrenska University Hospital, Gothenburg
John Walton Muscular Dystrophy Research Centre, Newcastle
U.O.C. Neuropsichiatria Infantile, Roma
Hospital Sant Joan de Déu Neuropediatra, Barcelona
Hospital La Fe de Valencia, Valencia
Leeds Teaching Hospital NHS Trust, Leeds
UCL, National Hospital for Neurology and Neurosurgery, London
Great Ormond Street Hospital for Children, London
Robert Jones and Agnes Hunt Orthopaedic Hospital, Oswestry
Oxford University hospitals NHS Foundation Trust, Oxford
Royal Hallamshire Hospital, Sheffield
Lead Sponsor
Santhera Pharmaceuticals
INDUSTRY