35
Participants
Start Date
April 11, 2012
Primary Completion Date
April 28, 2022
Study Completion Date
April 28, 2022
Set of assessment tools
Institut de Myologie, Groupe Hospitalier Pitié Salpêtrière, Paris
Leiden University Medical Centre, Leiden
Radboud University Medical Centre, Nijmegen
Dubowitz Neuromuscular Centre, UCL-Institute of Child Health, London
John Walton Muscular Dystrophy Research Centre, Newcastle University, Newcastle
Association Française contre les Myopathies (AFM), Paris
OTHER
University of Newcastle Upon-Tyne
OTHER
Groupe Hospitalier Pitie-Salpetriere
OTHER
Leiden University Medical Center
OTHER
Radboud University Medical Center
OTHER
University College, London
OTHER