23
Participants
Start Date
April 30, 2016
Primary Completion Date
June 24, 2020
Study Completion Date
July 31, 2020
AX 250
Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human insulin-like growth factor 2 (rhNAGLU-IGF2)
Mackay Memorial Hospital, Taipei
Children's Hospital Oakland, Oakland
Fundación Cardio Infantil - Instituto de Cardiología, Bogotá
University Medical Center Hamburg Eppendorf, Department of Pediatrics, Hamburg
Hospital Clinico Universitario de Santiago, Santiago de Compostela
Gazi Üniversitesi Tıp Fakültesi, Ankara
Somers Clinical Research Facility, Great Ormond Street Hospital, London
Lead Sponsor
Allievex Corporation
INDUSTRY