NCT02725580View on ClinicalTrials.gov

Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

13

Participants

Timeline

Start Date

March 9, 2016

Primary Completion Date

October 27, 2021

Study Completion Date

October 27, 2021

Conditions
Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Interventions
GENETIC

AT-GTX-501

CLN6 Gene delivered by Self-Complementary AAV9

Trial Locations (1)

43205

Nationwide Children's Hosptial, Columbus

Sponsors
All Listed Sponsors
lead

Amicus Therapeutics

INDUSTRY