GBE Deficiency (GSD IV and APBD) Natural History Study

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

December 31, 2015

Primary Completion Date

December 31, 2035

Study Completion Date

December 31, 2035

Conditions
Glycogen Storage Disease Type IVAdult Polyglucosan Body DiseaseGSD4GSD IVAPBD
Interventions
OTHER

No intervention

This is an observational study that consists of data abstraction from patient medical records.

Trial Locations (1)

27710

RECRUITING

Duke University Medical Center, Durham

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Duke University

OTHER

NCT02683512 - GBE Deficiency (GSD IV and APBD) Natural History Study | Biotech Hunter | Biotech Hunter