First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221

University of Pittsburgh, Pittsburgh

Perelman Center for Advanced Medicine, Philadelphia

Abramson Cancer Center Chester County Hospital, West Chester

Lysosomal & Rare Disorders Research & Treatment Center (LDRTC), Fairfax

Duke University Medical Center, Durham

Emory University Division of Medical Genetics, Decatur

University of Florida, Gainesville

University Children's Hospital Department of Neuropediatrics and Inborn Metabolic Disorders, St. Josefs-Hospital, Bochum

Infusion Associates, Grand Rapids

Great Falls Clinic, LLP, Great Falls

Friedrich-Baur-Institure, Dep of Neurology - University Munich, Munich

Neuromuscular Research Centre, Phoenix

University of California Irvine, Orange

Rutgers New Jersey Medical School, Newark

Womens & Childrens Hospital, Adelaide, North Adelaide

Erasmus Medical Center, Rotterdam

School of Medicine, University of Auckland, Auckland

University Hospital Birmingham NHS Foundation Trust, Queen Elizabeth Medical Center, Birmingham

Salford Royal NHS Foundation Trust, Salford