Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MOCD) Type A

PHASE2/PHASE3CompletedINTERVENTIONAL
Enrollment

5

Participants

Timeline

Start Date

May 31, 2016

Primary Completion Date

September 30, 2022

Study Completion Date

October 31, 2022

Conditions
Molybdenum Cofactor Deficiency, Type A
Interventions
DRUG

ORGN001 (formerly ALXN1101)

Trial Locations (11)

18341

HaEmek Medical Center, Afula

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

48201

Children's Hosptial of Michigan, Detroit

53226-4874

Children's Hospital of Wisconsin, Milwaukee

Unknown

Stavanger Universitetssjukehus, Stavanger

Gazi University, Ankara

Great Ormond Street Hosptial, London

08950

Hospital Sant Joan de Deu, Esplugues de Llobregat

06100

Hacettepe University of Medicine, Ankara

07058

Akdeniz University Medical Faculty, Antalya

M13 9WL

Willink Biochemical Genetics Unit, Manchester

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Origin Biosciences

INDUSTRY