5
Participants
Start Date
May 31, 2016
Primary Completion Date
September 30, 2022
Study Completion Date
October 31, 2022
ORGN001 (formerly ALXN1101)
HaEmek Medical Center, Afula
Cincinnati Children's Hospital Medical Center, Cincinnati
Children's Hosptial of Michigan, Detroit
Children's Hospital of Wisconsin, Milwaukee
Stavanger Universitetssjukehus, Stavanger
Gazi University, Ankara
Great Ormond Street Hosptial, London
Hospital Sant Joan de Deu, Esplugues de Llobregat
Hacettepe University of Medicine, Ankara
Akdeniz University Medical Faculty, Antalya
Willink Biochemical Genetics Unit, Manchester
Lead Sponsor
Origin Biosciences
INDUSTRY