Tools for Therapeutic Evaluation in Charcot-Marie-Tooth Disease Type 1A: Outcome Measures and Biomarkers

NAActive, not recruitingINTERVENTIONAL
Enrollment

80

Participants

Timeline

Start Date

June 6, 2016

Primary Completion Date

June 5, 2026

Study Completion Date

December 5, 2027

Conditions
Charcot-Marie-Tooth Disease Type 1A
Interventions
OTHER

Clinical evaluation

OTHER

electrophysiological record

OTHER

Muscle MRI

OTHER

blood samples analysis

Trial Locations (2)

13010

Assistance Publique Hôpitaux de Marseille, Marseille

34285

CHU Gui de Chauliac, CHU MONTPELLIER, Montpellier

All Listed Sponsors
lead

Assistance Publique Hopitaux De Marseille

OTHER