Amifampridine Phosphate for the Treatment of Congenital Myasthenic Syndromes

PHASE3CompletedINTERVENTIONAL
Enrollment

20

Participants

Timeline

Start Date

January 31, 2016

Primary Completion Date

August 31, 2019

Study Completion Date

October 31, 2019

Conditions
Myasthenic Syndromes, Congenital
Interventions
DRUG

amifampridine phosphate

Amifampridine phosphate tablets 10 mg will be provided in round, white-scored tablets, and containing amifampridine phosphate formulated to be the equivalent of 10 mg amifampridine base per tablet.

DRUG

Placebo

A placebo equivalent will be provided as tablets indistinguishable from the amifampridine phosphate tablets. The placebo will be administered consistent with the dose regimen of amifampridine phosphate.

Trial Locations (4)

21287

Johns Hopkins Pediatric Neurology, Baltimore

43221

Ohio State University, Columbus

90095

UCLA Department of Neurology, Los Angeles

02115

Boston Children's Hospital, Boston

Sponsors
All Listed Sponsors
lead

Catalyst Pharmaceuticals, Inc.

INDUSTRY

NCT02562066 - Amifampridine Phosphate for the Treatment of Congenital Myasthenic Syndromes | Biotech Hunter | Biotech Hunter