10
Participants
Start Date
May 31, 2015
Primary Completion Date
December 30, 2016
Study Completion Date
December 30, 2016
HT-100
HT-100 is Akashi Therapeutics' proprietary delayed-release formulation of halofuginone hydrobromide, a small molecule therapeutic with anti-fibrotic properties. May be administered in either fed or fasted state. Not mutation specific.
Kennedy Krieger Institute, Johns Hopkins School of Medicine, Baltimore
Nationwide Children's Hospital, Columbus
Cincinnati Children's Hospital Medical Center, Cincinnati
Washington University School of Medicine, St Louis
University of California, Davis Medical Center, Sacramento
Lead Sponsor
Akashi Therapeutics
INDUSTRY