Extension Study of Ataluren in Participants With Nonsense Mutation Cystic Fibrosis

PHASE3TerminatedINTERVENTIONAL
Enrollment

246

Participants

Timeline

Start Date

August 31, 2015

Primary Completion Date

June 2, 2017

Study Completion Date

June 2, 2017

Conditions
Cystic Fibrosis
Interventions
DRUG

Ataluren

Ataluren will be provided as a vanilla-flavored powder to be mixed with water or milk.

Trial Locations (70)

1

Universitatsklinikum Jena, Jena

4

Ospedale Pediatrico Bambino Gesu, Rome

15

Hopital Universitaire des Enfants Reine Fabiola, Brussels

71

Azienda Ospedaliero Universitaria Ospedall Riuniti di Acona-Umberto I G.M. Lancisi G. Salesi, Ancona

541

Ippokratio General Hospital Of Thessaloniki, Thessaloniki

1090

University Hospital Brussels, Brussels

1330

Hospital de Ninos Ricardo Gutierrez, Buenos Aires

3000

University Hospital Leuven, Leuven

4032

Prince Charles Hospital, Chermside

5000

Royal Adelaide Hospital, Adelaide

6840

Princess Margaret Hospital, Perth

10011

Beth Israel Medical Center, New York

10016

New York University Langone Medical Center, New York

10032

Columbia University Medical Center, New York

10117

Charite-Universitatsmedizin Berlin, Berlin

17033

Penn State Milton S. Hershey Medical Center, Hershey

19129

Drexel University College of Medicine, Philadelphia

20122

Lombardia Cystic Fibrosis Center, Milan

29001

Hospital Regional Universitario de Malaga, Málaga

29684

Centre de Perharidy, Roscoff

31096

Meyer Children's Hospital, Haifa

32207

Nemours Children's Clinic, Jacksonville

33136

University of Miami, Miami

33155

Miami Children's Hospital, Miami

33701

All Children's Hospital, St. Petersburg

34295

Hoptial Arnaud de Villeneuve, Montpellier

35233

University of Alabama at Birmingham, Birmingham

41013

Hospital Universitario Virgen del Rocio, Seville

44791

St. Josef Hospital GmbH, Bochum

45221

University of Cincinnati, Cincinnati

46202

Indiana University, Indianapolis

50139

Azienda Ospedaliera A Meyer, Florence

50937

University of Cologne Children's Hospital, Cologne

53226

Childrens Hospital of Wisconsin, Milwaukee

60590

Christiane Herzog CF-Zentrum, Frankfurt am Main

60611

Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

Washington University, St Louis

75015

Hopital Necker - Enfants Malades, Paris

75708

University of Texas Health Science Center, Tyler

77094

Texas Children's Hospital, Houston

80045

Children's Hospital Colorado, Aurora

80337

Dr. Von Haunersches Kinderspital, München

80539

LMU Klinikum der Universitat Muchen, Munich

90027

Children's Hospital Los Angeles, Los Angeles

90806

Miller Children's Hospital Long Beach, Long Beach

91240

Hadassah University Hospital, Jerusalem

94304

Stanford University-Children's Hospital, Palo Alto

94609

Children's Hospital and Research Center at Oakland, Oakland

97448

Centre Hospitalier Regional Sud Reunion, Saint-Pierre

02115

Children's Hospital Boston, Boston

07960

Morristown Medical Center, Morristown

Unknown

Hospital Universitario Austral, Buenos Aires

Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul, Porto Alegre

University Mulitiprofile Hospital for Active Treatment Sveti Georgi EAD, Plovdiv

University Multiprofile Hospital for Active Treatment Aleksandrovska EAD, Sofia

Azienda Ospedaliera di Verona, Verona

Szpital Dzieciecy Polanki im Macieja Plazynskiego w Gdansku, Gdansk

H2W 1R7

Clinical Research Institute of Montreal, Montreal

M5G 1X8

University of Toronto Hospital for Sick Children, Toronto

V6H 3V4

British Columbia Children's Hospital, Vancouver

00161

Azienda Policlinico Umberto I, Rome

2545 CH

Hagaziekenhuis, s-Gravenweg

6525 GA

Radboud University, Nijmegen

01-211

Institute of Mother and Child, Warsaw

08035

Hospital Universitario Vall d'Hebron, Barcelona

Hospital University, Barcelona

08950

Hospital San Juan, Esplugues de Llobregat

08208

Hospital de Sabadell, Consorci Sanitari Parc Tauli, Sabadell

LS9 7TF

St James University Hospital, Leeds

SW3 6NP

Royal Brompton Hospital, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PTC Therapeutics

INDUSTRY

NCT02456103 - Extension Study of Ataluren in Participants With Nonsense Mutation Cystic Fibrosis | Biotech Hunter | Biotech Hunter