246
Participants
Start Date
August 31, 2015
Primary Completion Date
June 2, 2017
Study Completion Date
June 2, 2017
Ataluren
Ataluren will be provided as a vanilla-flavored powder to be mixed with water or milk.
Universitatsklinikum Jena, Jena
Ospedale Pediatrico Bambino Gesu, Rome
Hopital Universitaire des Enfants Reine Fabiola, Brussels
Azienda Ospedaliero Universitaria Ospedall Riuniti di Acona-Umberto I G.M. Lancisi G. Salesi, Ancona
Ippokratio General Hospital Of Thessaloniki, Thessaloniki
University Hospital Brussels, Brussels
Hospital de Ninos Ricardo Gutierrez, Buenos Aires
University Hospital Leuven, Leuven
Prince Charles Hospital, Chermside
Royal Adelaide Hospital, Adelaide
Princess Margaret Hospital, Perth
Beth Israel Medical Center, New York
New York University Langone Medical Center, New York
Columbia University Medical Center, New York
Charite-Universitatsmedizin Berlin, Berlin
Penn State Milton S. Hershey Medical Center, Hershey
Drexel University College of Medicine, Philadelphia
Lombardia Cystic Fibrosis Center, Milan
Hospital Regional Universitario de Malaga, Málaga
Centre de Perharidy, Roscoff
Meyer Children's Hospital, Haifa
Nemours Children's Clinic, Jacksonville
University of Miami, Miami
Miami Children's Hospital, Miami
All Children's Hospital, St. Petersburg
Hoptial Arnaud de Villeneuve, Montpellier
University of Alabama at Birmingham, Birmingham
Hospital Universitario Virgen del Rocio, Seville
St. Josef Hospital GmbH, Bochum
University of Cincinnati, Cincinnati
Indiana University, Indianapolis
Azienda Ospedaliera A Meyer, Florence
University of Cologne Children's Hospital, Cologne
Childrens Hospital of Wisconsin, Milwaukee
Christiane Herzog CF-Zentrum, Frankfurt am Main
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University, St Louis
Hopital Necker - Enfants Malades, Paris
University of Texas Health Science Center, Tyler
Texas Children's Hospital, Houston
Children's Hospital Colorado, Aurora
Dr. Von Haunersches Kinderspital, München
LMU Klinikum der Universitat Muchen, Munich
Children's Hospital Los Angeles, Los Angeles
Miller Children's Hospital Long Beach, Long Beach
Hadassah University Hospital, Jerusalem
Stanford University-Children's Hospital, Palo Alto
Children's Hospital and Research Center at Oakland, Oakland
Centre Hospitalier Regional Sud Reunion, Saint-Pierre
Children's Hospital Boston, Boston
Morristown Medical Center, Morristown
Hospital Universitario Austral, Buenos Aires
Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul, Porto Alegre
University Mulitiprofile Hospital for Active Treatment Sveti Georgi EAD, Plovdiv
University Multiprofile Hospital for Active Treatment Aleksandrovska EAD, Sofia
Azienda Ospedaliera di Verona, Verona
Szpital Dzieciecy Polanki im Macieja Plazynskiego w Gdansku, Gdansk
Clinical Research Institute of Montreal, Montreal
University of Toronto Hospital for Sick Children, Toronto
British Columbia Children's Hospital, Vancouver
Azienda Policlinico Umberto I, Rome
Hagaziekenhuis, s-Gravenweg
Radboud University, Nijmegen
Institute of Mother and Child, Warsaw
Hospital Universitario Vall d'Hebron, Barcelona
Hospital University, Barcelona
Hospital San Juan, Esplugues de Llobregat
Hospital de Sabadell, Consorci Sanitari Parc Tauli, Sabadell
St James University Hospital, Leeds
Royal Brompton Hospital, London
Lead Sponsor
PTC Therapeutics
INDUSTRY