320
Participants
Start Date
February 28, 2015
Primary Completion Date
July 31, 2018
Study Completion Date
July 31, 2018
The University of North Carolina at Chapel Hill, Chapel Hill
Riley Hospital for Children, Indianapolis
Washington University, St. Louis, St Louis
The Children's Hospital, Denver, Aurora
Stanford University, Palo Alto
Children's Hospital and Regional Medical Center, Seattle, Seattle
The Hospital for Sick Children, Toronto
McGill University, Montreal
Rare Diseases Clinical Research Network
NETWORK
National Institutes of Health (NIH)
NIH
National Heart, Lung, and Blood Institute (NHLBI)
NIH
University of North Carolina, Chapel Hill
OTHER