NCT02376816View on ClinicalTrials.gov

Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy

PHASE1CompletedINTERVENTIONAL
Enrollment

2

Participants

Timeline

Start Date

March 31, 2015

Primary Completion Date

September 30, 2017

Study Completion Date

September 30, 2017

Conditions
Duchenne Muscular Dystrophy
Interventions
BIOLOGICAL

rAAVrh74.MCK.micro-Dystrophin

"Recombinant adeno-associated virus carrying a truncated micro dystrophin transgene under control of a muscle specific MCK promoter."

Trial Locations (1)

43205

Nationwide Children's Hospital, Columbus

All Listed Sponsors
collaborator

Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)

NIH

lead

Jerry R. Mendell

OTHER

NCT02376816 - Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy | Biotech Hunter | Biotech Hunter