Open-Label PoC Trial of Ganaxolone in Children With PCDH19 Female Pediatric Epilepsy and Other Rare Genetic Epilepsies

PHASE2CompletedINTERVENTIONAL
Enrollment

30

Participants

Timeline

Start Date

November 6, 2015

Primary Completion Date

January 16, 2018

Study Completion Date

January 4, 2019

Conditions
Epilepsy
Interventions
DRUG

Ganaxolone

oral suspension or capsules

Trial Locations (10)

30093

Center for Rare Neurological Diseases, Norcross

43205

Nationwide Children's Hospital, Columbus

46239

JWM Neurology, Indianapolis

85016

Phoenix Children's Hospital, Phoenix

94143

University of California San Francisco, San Francisco

95816

Sutter Institute for Medical Research, Sacramento

02115

Boston Children's Hospital, Boston

07601

Northeast Regional Epilepsy Group, Hackensack

07039

Institute of Neurology and Neurosurgery at St. Barnabas, Livingston

00165

Bambino Gesu Children's Hospital, IRCCS, Rome

Sponsors
All Listed Sponsors
lead

Marinus Pharmaceuticals

INDUSTRY