3
Participants
Start Date
January 31, 2015
Primary Completion Date
November 30, 2017
Study Completion Date
November 30, 2017
rAAV1.CMV.huFollistin344
Six DMD patients will receive rAAV1.CMV.huFollistatin344 to both limbs by multiple injections to gluteal muscles, quadriceps and tibialis anterior muscles.
Nationwide Children's Hospital, Columbus
Collaborators (2)
Duchenne Alliance
OTHER
Milo Therapeutics
INDUSTRY
Jerry R. Mendell
OTHER