NCT02350816View on ClinicalTrials.gov

An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093.

PHASE2TerminatedINTERVENTIONAL
Enrollment

17

Participants

Timeline

Start Date

April 8, 2015

Primary Completion Date

April 12, 2019

Study Completion Date

April 12, 2019

Conditions
Sanfilippo SyndromeMucopolysaccharidosis (MPS)
Interventions
DRUG

HGT-1410

HGT-1410 administered according to Patient Group assignment.

Trial Locations (8)

20246

Universitätsklinikum Hamburg Eppendorf, Hamburg

20900

Azienda Socio Sanitaria Territoriale - Asst di Monza, Monza

22660

Academisch Medisch Centrum Amsterdam, Amsterdam

27514

University of North Carolina at Chapel Hill, Chapel Hill

55455

University of Minnesota, Minneapolis

94270

Chu Bicetre, Le Kremlin-Bicêtre, Paris

08035

Hospital Universitario Vall D'hebron - Ppds, Barcelona

WC1N 3JH

Great Ormond Street Hospital, London

Sponsors

Lead Sponsor

Shire
All Listed Sponsors
lead

Shire

INDUSTRY