Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD)

PHASE2TerminatedINTERVENTIONAL
Enrollment

15

Participants

Timeline

Start Date

December 31, 2014

Primary Completion Date

July 1, 2016

Study Completion Date

August 31, 2016

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

PRO044 SC 6 mg/kg

DRUG

PRO044 IV 6 mg/kg

DRUG

PRO044 IV 9 mg/kg

Trial Locations (5)

Unknown

UZ Leuven, Leuven

S.Anna Hospital, Ferrara

Policlinico Universitario Agostino Gemelli, Roma

Leids Universitair Medisch Centrum, Leiden

Drottning Silvias Barn- ochungdomssjukhus, Gothenburg

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY