A Safety andTolerability Study of Multiple Doses of ISIS-DMPKRx in Adults With Myotonic Dystrophy Type 1

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

48

Participants

Timeline

Start Date

December 31, 2014

Primary Completion Date

July 31, 2016

Study Completion Date

August 31, 2016

Conditions
Myotonic Dystrophy Type 1
Interventions
DRUG

IONIS-DMPKRx

Drug

DRUG

Placebo

Placebo

Trial Locations (8)

14642

University of Rochester, Rochester

21205

Kennedy Krieger Institute, Baltimore

32610

University of Florida, Gainesville

43221

The Ohio State University, Columbus

66103

University of Kansas Medical Center, Kansas City

77030

Houston Methodist, Houston

84132

University of Utah, Salt Lake City

94305

Stanford University Medical Center, Stanford

Sponsors
All Listed Sponsors
lead

Ionis Pharmaceuticals, Inc.

INDUSTRY