48
Participants
Start Date
December 31, 2014
Primary Completion Date
July 31, 2016
Study Completion Date
August 31, 2016
IONIS-DMPKRx
Drug
Placebo
Placebo
University of Rochester, Rochester
Kennedy Krieger Institute, Baltimore
University of Florida, Gainesville
The Ohio State University, Columbus
University of Kansas Medical Center, Kansas City
Houston Methodist, Houston
University of Utah, Salt Lake City
Stanford University Medical Center, Stanford
Lead Sponsor
Ionis Pharmaceuticals, Inc.
INDUSTRY