39
Participants
Start Date
January 13, 2015
Primary Completion Date
March 25, 2019
Study Completion Date
March 25, 2019
Placebo
SRP-4053 placebo-matching solution for IV infusion.
SRP-4053
SRP-4053 (golodirsen) solution for IV infusion.
Institute de Myologie, Paris
Boston Children's Hospital, Boston
Policlinico Universitario A Gemelli, Rome
Great Ormond Street Hospital for Children NHS Foundation Trust, London
Newcastle University Hospital, Newcastle
Institut de Myologie, France
OTHER
Consultants for Research in Imaging and Spectroscopy
OTHER
Great Ormond Street Hospital for Children NHS Foundation Trust
OTHER
Catholic University of the Sacred Heart
OTHER
Royal Holloway University
OTHER
SYSNAV
INDUSTRY
University College, London
OTHER
University of Newcastle Upon-Tyne
OTHER
Sarepta Therapeutics, Inc.
INDUSTRY