121
Participants
Start Date
November 24, 2014
Primary Completion Date
April 30, 2018
Study Completion Date
November 23, 2018
PF-06252616
PF-06252616 IV Infusion, 3 dose levels (5mg/kg, 20 mg/kg and 40 mg/kg) will be investigated within each subject
Placebo
Clinical Densitometry and Bone Metabolic Disease Department, General and Clinical Pathology Clinic, Sofia
Hospital Pharmacy, UMHAT Alexandrovska, Sofia
Imaging Diagnostic Clinic,UMHAT Alexandrovska, Sofia
Neurology Disease Clinic,UMHAT Alexandrovska, Sofia
UMHAT Alexandrovska Cardiology Department,Internal Diseases Propaedeutic Clinic, Sofia
Lady Cilento Children's Hospital, South Brisbane
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
UOC Farmacia-Istituto Gianna Gaslini, Istituto Pediatrico di Ricovero e Cura a Carattere Scientifico, Genova
UOC Medicina Fisica Riabilitativa, Genova
UOC Neurologia Pediatrica e Malattie Muscolari, Genova
UOC Radiologia-Istituto Gianna. Gaslini, Istituto Pediatrico di Ricovero e Cura a Carattere, Genova
UOS Dipartimentale Endocrinologia Clinica Sperimentale, Genova
The Children's Hospital of Philadelphia, Philadelphia
Kennedy Krieger Institute Out-patient center, Baltimore
Kennedy Krieger Institute, Baltimore
Johns Hopkins Hospital, Baltimore
Johns Hopkins Investigational Drug Service, Baltimore
Duke University Medical Center,Lenox Baker Children's Hospital, Durham
Duke University, Investigational Drug Pharmacy, Durham
Shriners Hospitals for Children - Tampa, Tampa
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Iowa ICTS, Iowa City
University of Minnesota Masonic Children's Hospital, Minneapolis
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
St Louis Children's Hospital, St Louis
University of Kansas Medical Center, Landon Center on Aging, Kansas City
University of Kansas Medical Center, Kansas City
KU Clinical Research Center, Clinical and Translational Science Unit(CTSU), Fairway
University of Kansas-Clinical Research Center, Investigational Pharmacy, Fairway
Children's Hospital Colorado, Aurora
Center for Clinical and Translational Sciences, Salt Lake City
Utah Center for Advanced Imaging and Research (UCAIR), Salt Lake City
Investigational Drug Services, Salt Lake City
University of Utah, Department of Neurology, Salt Lake City
University of Utah Medical Center, Salt Lake City
University of Utah School of Medicine, Salt Lake City
Ronald Reagan UCLA Medical Center, Los Angeles
Ronald Reagan UCLA Pharmacy, Los Angeles
UCLA (David Geffen School of Medicine), Los Angeles
University of California, Davis Medical Center, Sacramento
Massachusetts General Hospital, Boston
Alberta Children's Hospital, Calgary
UBC Children's and Women's Health Center of British Columbia, Vancouver
Children's Hospital- London Health Sciences Centre, London
CHU Sainte-Justine, Montreal
Dipartimento Pediatrico Universitario-Ospedaliero Endocrinologia, Rome
Farmacia Ospedaliera, IRCCS Ospedale Pediatrico Bambino Gesù, Padiglione Sant'Onofrio, Rome
Malattie Neuromuscolari e Neurodegenerative, IRCCS Ospedale Pediatrico Bambino Gesù, Rome
Ospedale Pediatrico Bambino Gesù - Centro Trial, DPUO - Padiglione Salviati, Rome
U.O.C Farmacia, Rome
U.O.C. Neuropsichiatria Infantile, Fondazione Policlinico, Rome
Hyogo college of medicine hospital, Hyōgo
National Center of Neurology and Psychiatry, Tokyo
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie Apteka Szpitalna Blok F, Warsaw
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie, I Katedra i Klinika Kardiologii, Warsaw
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie, II Zaklad Radiologii Klinicznej, Warsaw
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie, Klinika Neurologii, Warsaw
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie, Laboratorium Centralne, Warsaw
MTZ Clinical Research Sp.z o.o., Warsaw
Alder Hey Children's NHS Foundation Trust, Liverpool
Alder Hey Children's NHS Foundation Trust, Liverpool
Dubowitz Neuromuscular Centre Institute of Child Health, London
Great Ormond Street Hospital, London
Institute of Genetic Medicine, Muscle Team, Newcastle upon Tyne
Clinical Research Facility, Newcastle upon Tyne
Royal Victoria Infirmary Research Pharmacy, Newcastle upon Tyne
Lead Sponsor
Pfizer
INDUSTRY