24
Participants
Start Date
December 31, 2014
Primary Completion Date
August 24, 2017
Study Completion Date
August 24, 2017
Deflazacort
Deflazacort, a glucocorticoid with anti-inflammatory and immunosuppressive effects, is used in treating a variety of diseases. Pharmacologically it is an inactive pro-drug which is metabolized rapidly to the active drug 21-desacetyldeflazacort.
University of Rochester, Rochester
Lurie Children's Hospital, Chicago
University of Utah, Salt Lake City
UCLA, Los Angeles
Lead Sponsor
PTC Therapeutics
INDUSTRY