Study of Eteplirsen in DMD Patients

PHASE3CompletedINTERVENTIONAL
Enrollment

109

Participants

Timeline

Start Date

November 17, 2014

Primary Completion Date

June 14, 2019

Study Completion Date

June 14, 2019

Conditions
Duchenne Muscular Dystrophy (DMD)
Interventions
DRUG

eteplirsen

Eteplirsen 30 mg/kg will be administered as an IV infusion once a week for 96 weeks, followed by a safety extension (not to exceed 48 weeks).

Trial Locations (37)

10032

Columbia University Medical Center, New York

14642

University of Rochester Clinical Research Center, Rochester

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

17033

Penn State Hershey Medical Center, Hershey

19104

Children's Hospital of Philadelphia, Philadelphia

20010

Children's National Health System, Washington D.C.

21205

Kennedy Krieger Institute, Baltimore

28207

Levine Childrens Hospital, Carolinas Medical Center, Charlotte

30318

Rare Disease Research Center, Atlanta

30324

Emory University, Atlanta

32561

NW FL Clinical Research Group, LLC, Gulf Breeze

32610

The University of Florida, Powell Gene Therapy Center, Gainesville

32827

Nemours Children's Hospital, Orlando

37232

Vanderbilt University Medical Center, Nashville

43205

Nationwide Children's Hospital, Columbus

45229

Cincinnati Children's Hospital Medical Center (CCHMC), Cincinnati

48201

Children's Hospital of Michigan, Detroit

52242

University of Iowa Children's Hospital, Iowa City

55455

University of Minnesota, Minneapolis

60611

Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago

63110

St. Louis Children's Hospital, St Louis

66160

University of Kansas Medical Center, Kansas City

75390

The University of Texas Southwestern Medical Center, Dallas

77030

Texas Children's Hospital, Houston

80045

Children's Hospital Colorado, Aurora

84132

University of Utah, Salt Lake City

85028

Neuromuscular Research Center, Phoenix

90095

David Geffen School of Medicine at UCLA, Los Angeles

92130

Rady Children's Hospital, U.C. San Diego, San Diego

94305

Stanford University School of Medicine/Medical Center, Stanford

95817

University of California, Davis Medical Center, Sacramento

97239

Shriners Hospital for Children, Portland

98105

Seattle Children's Hospital, Seattle

06106

Connecticut Children's Medical Center, Hartford

02114

Massachusetts General Hospital, Boston

02115

Children's Hospital Boston, Boston

03756

Dartmouth-Hitchcock Medical Center, Lebanon

All Listed Sponsors
lead

Sarepta Therapeutics, Inc.

INDUSTRY

NCT02255552 - Study of Eteplirsen in DMD Patients | Biotech Hunter | Biotech Hunter