Safety and Efficacy Study of Sebelipase Alfa in Participants With Lysosomal Acid Lipase Deficiency

PHASE2CompletedINTERVENTIONAL
Enrollment

31

Participants

Timeline

Start Date

June 24, 2014

Primary Completion Date

December 28, 2017

Study Completion Date

December 28, 2017

Conditions
Lysosomal Acid Lipase Deficiency
Interventions
DRUG

Sebelipase Alfa

IV infusion of sebelipase alfa

Trial Locations (19)

1105

Amsterdam

1200

Brussels

2100

Copenhagen

10000

Zagreb

15006

A Coruña

28046

Madrid

35128

Padua

45229

Cincinnati

60611

Chicago

71103

Shreveport

79106

Freiburg im Breisgau

117997

Moscow

NSW 2145

Westmead

04024-002

São Paulo

B3H 1V7

Halifax

06720

Mexico City

08036

Barcelona

01300

Balcalı

B4 6NH

Birmingham

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY