Open-Label Study of Uridine Triacetate in Pediatric Patients With Hereditary Orotic Aciduria

PHASE3CompletedINTERVENTIONAL
Enrollment

4

Participants

Timeline

Start Date

April 30, 2014

Primary Completion Date

December 31, 2014

Study Completion Date

September 8, 2016

Conditions
Hereditary Orotic Aciduria
Interventions
DRUG

uridine triacetate

Trial Locations (2)

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

48201

Children's Hospital of Michigan - Specialty Center Detroit, Detroit

All Listed Sponsors
lead

Wellstat Therapeutics

INDUSTRY

NCT02110147 - Open-Label Study of Uridine Triacetate in Pediatric Patients With Hereditary Orotic Aciduria | Biotech Hunter | Biotech Hunter