61
Participants
Start Date
May 23, 2014
Primary Completion Date
June 5, 2017
Study Completion Date
June 5, 2017
Ataluren
Ataluren will be administered per dose and schedule specified in the arm.
Beth Israel Medical Center, New York
Hôpital des Enfants, Toulouse
University of Alabama-Birmingham, Birmingham
Rainbow Babies & Children's Hospital, Cleveland
Children's Hospital Chicago, Chicago
Denver Children's Hospital, Aurora
Miller Children's Hospital Long Beach, Long Beach
Hadassah University Hospital - Mount Scopus, Jerusalem
Children's Hospital Boston, Boston
Hôpital Universitaire des Enfants Reine Fabiola, Brussels
University Hospital Brussels, Brussels
University Hospital Leuven, Leuven
Hôpital Necker - Enfants Malades, Paris
Università La Sapienza, Roma
Azienda Ospedaliera di Verona, Verona
Hospital Universitario La Paz, Madrid
Karolinska University Hospital, Huddinge, Stockholm
Lead Sponsor
PTC Therapeutics
INDUSTRY