219
Participants
Start Date
March 20, 2014
Primary Completion Date
June 12, 2018
Study Completion Date
June 12, 2018
Ataluren
Ataluren will be administered per the dose and schedule specified in the arm.
CHUV Lausanne, Lausanne
Aleksandrovska Hospital, Sofia
The Children's Hospital at Westmead, Westmead
UZ Leuven, Leuven
The Royal Children's Hospital, Parkville
Columbia University College of Physicians & Surgeons, New York
Hospital de la Timone, Marseille
Children's Hospital of Pittsburgh, Pittsburgh
Astrid Lindgren Childrens Hospital, Stockholm
The Children's Hospital of Philadelphia, Philadelphia
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico di Milano, Milan
Child Neurology Center of Northwest Florida, Gulf Breeze
Erciyes University Faculty of Medicine, Talas/Kayseri
Nationwide Children's Hospital, Columbus
CHU de Nantes, Nantes
Universitaetsklinikum Essen, Essen
Children's Hospital Cincinnati, Cincinnati
Hospital Universitari i Politecnic la Fe, Valencia
University of Iowa, Iowa City
University of Minnesota, Minneapolis
Rush University Medical Center, Chicago
Washington University School of Medicine, Division of Endocrinology, Metabolism and Lipid Research, St Louis
University of Kansas Medical Center, Kansas City
Hopital Necker - Enfants Malades, Paris
Childrens Medical Center Dallas, Texas, Dallas
Groupe Hospitalier Pitie-Salpetriere, Paris
Texas Children's Hospital, Houston
University Medical Center Freiburg, Freiburg im Breisgau
Children's Hospital Colorado - Center for Cancer and Blood Disorders, Aurora
Universitat Munchen - von Haunersche Kinder Clinic, München
University of Utah, Salt Lake City
University of California, Los Angeles, Los Angeles
Hadassah University Hospital, Jerusalem
Stanford University Medical Center, Stanford
UC Davis Medical Center, Sacramento
Oregon Health & Science University, Portland
Seattle Children's Hospital - Childhood Cancer and Blood Disorders, Seattle
Policlinico Universitario G. Martino, Sicily
Hospital Clinico Universidad Catolica, Santiago
Children's Hospital Boston, Boston
Universidade Federal do Rio de Janeiro - Instituto de Puericultura e Pediatria Martagao Gesteira, Rio de Janeiro
Sao Paulo University -HC/FMUSP, São Paulo
Alberta Children's Hospital, Calgary
British Columbia Children's Hospital, Vancouver
Children's Hospital of Western Ontario, London
Hospital Luis Calvo Mackenna, Santiago
University Hospital Brno, Brno
Motol University Hospital, Prague
Bambino Gesu Hospital, Rome
U.O. Complessa di Neuropsichiatria Infantile, Rome
Medical University of Warsaw, Warsaw
Seoul National University Hospital, Seoul
Hospital Sant Joan de Deu, Barcelona
Queen Silvia Children's Hospital, Gothenburg
Hacettepe Childrens Hospital, Ankara
University College London Institute of Child Health, London
Royal Manchester Children's Hospital, Manchester
The Newcastle upon Tyne Hospitals, NHS Foundation Trust, Newcastle upon Tyne
Lead Sponsor
PTC Therapeutics
INDUSTRY