Safety Evaluation of Gene Therapy in Leber Hereditary Optic Neuropathy (LHON) Patients

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

19

Participants

Timeline

Start Date

February 13, 2014

Primary Completion Date

June 25, 2020

Study Completion Date

June 25, 2020

Conditions
Leber Hereditary Optic Neuropathy
Interventions
GENETIC

GS010

Trial Locations (1)

75012

CIC du CHNO DES QUINZE-VINGTS, Paris

Sponsors

Lead Sponsor

All Listed Sponsors
lead

GenSight Biologics

INDUSTRY